Making a Difference for Patients:

It’s Up to U

At Ultragenyx, we strive to incorporate patient and family voices into everything we do. Watch our video celebrating how U motivate and inspire us every day.

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Latest Blog Post

Genetic Testing 101: Know Your Genes

Eighty percent of rare diseases are genetic.1 Genetic testing is a tool that can help identify these conditions in individuals and families. It helps empower people to make informed decisions about their health.

Your Voice Matters: We are Listening

Marah

A Sibling’s Journey

Franco

Raising a child with CTD

Michelle and Jake

Managing LC-FAOD Together

Braylee

Raising a child with LC-FAOD

Helen

An MPS VII Parent

Cheryl

Living with XLH

Tasia

Living with LC-FAOD

Dan

Living with TIO

David

Living with XLH

Eileen

Raising a Child with LC-FAOD

OTC

Ornithine Transcarbamylase Deficiency

GSDIa

Glycogen Storage Disease
Type Ia

Wilson Disease

Wilson Disease

GSDIII

Glycogen Storage Disease
Type III

Angelman Syndrome

Angelman Syndrome

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