Making a Difference for Patients:

It’s Up to U

At Ultragenyx, we strive to incorporate patient and family voices into everything we do. Watch our video celebrating how U motivate and inspire us every day.

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Latest Blog Post

Your Voice Matters: How to Engage with the FDA

The FDA you say? Yes! The Food and Drug Administration (FDA) is the regulatory agency in the United States that reviews and approves (foods and) medicines for use in people....

Your Voice Matters: We are Listening

Marah

A Sibling’s Journey

Franco

Raising a child with CTD

Michelle and Jake

Managing LC-FAOD Together

Braylee

Raising a child with LC-FAOD

Helen

An MPS VII Parent

Cheryl

Living with XLH

Tasia

Living with LC-FAOD

Dan

Living with TIO

David

Living with XLH

Eileen

Raising a Child with LC-FAOD

OTC

Ornithine Transcarbamylase Deficiency

GSDIa

Glycogen Storage Disease
Type Ia

Wilson Disease

Wilson Disease

GSDIII

Glycogen Storage Disease
Type III

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