Making a Difference for Patients:

It’s Up to U

At Ultragenyx, we strive to incorporate patient and family voices into everything we do. Watch our video celebrating how U motivate and inspire us every day.

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COVID-19 Resources & Information

Upcoming Events

  1. Jun 28

    Our Odyssey Virtual Meet-Ups

    Learn More
  2. Aug 3

    Rare Across America

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Latest Blog Post

Rare & Prepared: Emergency Planning for Individuals with Complex Healthcare Needs

According to the Federal Emergency Management Agency (FEMA), nearly half of U.S. adults do not have the resources and plans in place in the event of an emergency.1 Preparing for…

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Featured Educational Resources

Your Voice Matters: We are Listening

Marah

A Sibling’s Journey

Franco

Raising a child with CTD

Michelle and Jake

Managing LC-FAOD Together

Braylee

Raising a child with LC-FAOD

Helen

An MPS VII Parent

Cheryl

Living with XLH

Tasia

Living with LC-FAOD

Dan

Living with TIO

David

Living with XLH

Eileen

Raising a Child with LC-FAOD

OTC

Ornithine Transcarbamylase Deficiency

GSDIa

Glycogen Storage Disease
Type Ia

Wilson Disease

Wilson Disease

GSDIII

Glycogen Storage Disease
Type III

Angelman Syndrome

Angelman Syndrome

Click here to learn more about Ultragenyx’s response to the evolving COVID-19 pandemic.

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    You must be 18 years of age or older and a resident of the United States or its territories to register. By registering to receive these emails, you certify that you are 18 years of age or older, reside in the United States or its territories and are granting permission to receive general updates and news from Patient Advocacy at Ultragenyx.

    By providing your information you agree to allow Ultragenyx and its agents to collect the name and email address provided and to be contacted by Ultragenyx and its agents using this information in the future. Furthermore, you are agreeing that Ultragenyx and its agents may contact you by email. Ultragenyx will not sell, rent or otherwise distribute your name and email address provided.