Event dates may change due to the evolving COVID-19 pandemic. We encourage you to check specific event websites for the most up-to-date status.

If you would like to have your event added to the list, please contact patientadvocacy@ultragenyx.com.

Loading Events

« All Events

  • This event has passed.

Patient Perspectives on the Impact of Rare Diseases: Bridging the Commonalities

April 29, 2019


The U.S. Food and Drug Administration (FDA) is holding this public meeting to obtain patients’ and caregivers’ perspectives on the impact of rare diseases on daily life. While the differences between rare diseases are important, it is also important to understand the commonalities to help improve product development. The FDA’s goal for this meeting is to identify common issues and symptoms that can help advance medical product development, potentially through the creation of novel endpoints or trial designs that focus on similarities across a variety of rare diseases.

Register here


April 29, 2019